Twins and the Challenge of Spinal Muscular Atrophy: A Family’s Journey
Emma and Bartosz, twins diagnosed with Spinal Muscular Atrophy, highlight the urgent need for newborn screening in the UK.
Childhood dementia: The Heartbreaking Reality of : Leni Forrester’s Fight Against Sanfilippo Disease
Leni Forrester, just two years old, faces the devastating effects of childhood dementia due to Sanfilippo disease. Her family's fight for treatment highlights the urgency of research and funding.